⚡ Neurological / SeizureInjection (IV)
Zolgensma
Onasemnogene Abeparvovec
Gene therapy for spinal muscular atrophy (SMA) in pediatric patients less than 2 years old.
Form
Injection (IV)
Uses
1
Side effects
3
Category
Neurological
01
What is Zolgensma used for?
- Spinal muscular atrophy type 1 (SMA1)
02
Onasemnogene Abeparvovec side effects
The following side effects have been reported for Onasemnogene Abeparvovec. Their order does not indicate how often an effect occurs.
Elevated liver enzymes
Vomiting
Fever
03
Onasemnogene Abeparvovec warnings & precautions
- Black box: acute serious liver injury. Monitor liver function and platelet counts
- One-time administration only
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04
Frequently asked questions
05
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Disclaimer: This information is sourced from the FDA openFDA database and is provided for educational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment. Always consult your physician or pharmacist before starting or changing medication.