Neurological / SeizureInjection (IV)

    Zolgensma

    Onasemnogene Abeparvovec

    Gene therapy for spinal muscular atrophy (SMA) in pediatric patients less than 2 years old.

    Form

    Injection (IV)

    Uses

    1

    Side effects

    3

    Category

    Neurological

    01

    What is Zolgensma used for?

    • Spinal muscular atrophy type 1 (SMA1)
    02

    Onasemnogene Abeparvovec side effects

    Common side effects of Onasemnogene Abeparvovec include:

    Elevated liver enzymes
    Vomiting
    Fever
    CommonModerateLess common
    03

    Onasemnogene Abeparvovec warnings & precautions

    • Black box: acute serious liver injury. Monitor liver function and platelet counts
    • One-time administration only

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    04

    Frequently asked questions

    05

    Related medications

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    Disclaimer: This information is sourced from the FDA openFDA database and is provided for educational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment. Always consult your physician or pharmacist before starting or changing medication.