🔬 GastrointestinalCapsule

    Orfadin

    Nitisinone

    Enzyme inhibitor that blocks toxic metabolite accumulation in hereditary tyrosinemia type 1.

    Form

    Capsule

    Uses

    2

    Side effects

    5

    Category

    Gastrointestinal

    01

    What is Orfadin used for?

    • Hereditary tyrosinemia type 1
    • Alkaptonuria
    02

    Nitisinone side effects

    The following side effects have been reported for Nitisinone. Their order does not indicate how often an effect occurs.

    Elevated tyrosine levels
    Eye pain
    Corneal opacity
    Thrombocytopenia
    Leukopenia
    03

    Nitisinone warnings & precautions

    • Restrict dietary phenylalanine and tyrosine intake
    • Routine eye exams required
    • Monitor liver function and alpha-fetoprotein levels

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    04

    Frequently asked questions

    05

    Related medications

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    Disclaimer: This information is sourced from the FDA openFDA database and is provided for educational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment. Always consult your physician or pharmacist before starting or changing medication.