🔬 GastrointestinalCapsule

    Orfadin

    Nitisinone

    Enzyme inhibitor that blocks toxic metabolite accumulation in hereditary tyrosinemia type 1.

    Form

    Capsule

    Uses

    2

    Side effects

    5

    Category

    Gastrointestinal

    01

    What is Orfadin used for?

    • Hereditary tyrosinemia type 1
    • Alkaptonuria
    02

    Nitisinone side effects

    Common side effects of Nitisinone include:

    Elevated tyrosine levels
    Eye pain
    Corneal opacity
    Thrombocytopenia
    Leukopenia
    CommonModerateLess common
    03

    Nitisinone warnings & precautions

    • Restrict dietary phenylalanine and tyrosine intake
    • Routine eye exams required
    • Monitor liver function and alpha-fetoprotein levels

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    04

    Frequently asked questions

    05

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    Disclaimer: This information is sourced from the FDA openFDA database and is provided for educational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment. Always consult your physician or pharmacist before starting or changing medication.